- introduce a working ADA gene into their bone marrow stem cells
- provide them with daily injections of the ADA enzyme for the rest of their life
- create a vaccine against their own immune cells
- use monoclonal antibodies to suppress their immune system
A patient with severe combined immunodeficiency (SCID) lacks a functional gene for the enzyme adenosine deaminase (ADA). The goal of gene therapy for this patient is to:
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